Commentary on the new study published by the Verona CF Center on Shwachman-Diamond Syndrome
Ataluren Boosts Blood and Pancreas Health in Shwachman-Diamond
Ataluren Boosts Blood and Pancreas Health in Shwachman-Diamond
October – December 2025
14 October 2025
This document now lists ETI (Kaftrio), ivacaftor (Kalydeco) and pancreatic enzymes (e.g. Creon) as essential medicines.
Ataluren improves hematopoietic and pancreatic disorders in Shwachman-Diamond syndrome patients: a compassionate program case-series.
27-29 November 2025
27 September – 1 October 2025
22-25 October 2025, Seattle
16-17 May 2025, Verona
4-7 June 2025, Milan